Biochemical and clinical response after umbilical cord blood transplant in a boy with early childhood-onset beta-mannosidosis

Troy C Lund, Weston P. Miller, Julie Eisengart, Katrina Simmons, Laura Pollard, Deborah L. Renaud, David A. Wenger, Marc C. Patterson, Paul J. Orchard

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10 Scopus citations

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Medicine & Life Sciences