Abstract
The art and science of gene therapy has received much attention of late. The tragic death of 18-year-old Jesse Gelsinger, a volunteer in a Phase I clinical trial, has overshadowed the successful treatment of three children suffering from a rare but fatal immunological disease. In the light of the success and tragedy, it is timely to consider the challenges faced by gene therapy - a novel form of molecular medicine that may be poised to have an important impact on human health in the new millennium.
Original language | English (US) |
---|---|
Pages (from-to) | 91-99 |
Number of pages | 9 |
Journal | Nature Reviews Genetics |
Volume | 1 |
Issue number | 2 |
DOIs | |
State | Published - Nov 2000 |