GM1-gangliosidosis: The caregivers' assessments of symptom impact and most important symptoms to treat

Amanda Bingaman, Christine Waggoner, Sara M. Andrews, Diana Pangonis, Marie Trad, Roberto Giugliani, Ruben Giorgino, Jeanine Jarnes, Rojan Vakili, Victoria Ballard, Holly L. Peay

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Medicine & Life Sciences