Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A

Johnny Mahlangu, Radoslaw Kaczmarek, Annette Von Drygalski, Susan Shapiro, Sheng Chieh Chou, Margareth C. Ozelo, Gili Kenet, Flora Peyvandi, Michael Wang, Bella Madan, Nigel S. Key, Michael Laffan, Amy L. Dunn, Jane Mason, Doris V. Quon, Emily Symington, Andrew D. Leavitt, Johannes Oldenburg, Hervé Chambost, Mark T. RedingKala Jayaram, Hua Yu, Reena Mahajan, Konstantia Maria Chavele, Divya B. Reddy, Joshua Henshaw, Tara M. Robinson, Wing Yen Wong, Steven W. Pipe

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